یادداشتهای مربوط به کتابنامه ، واژه نامه و نمایه های داخل اثر
متن يادداشت
Includes bibliographical references and index.
یادداشتهای مربوط به مندرجات
متن يادداشت
Design and testing of regulatory cassettes for optimal activity in skeletal and cardiac muscles -- Codon optimization of the microdystrophin gene for Duchene muscular dystrophy gene therapy -- Monitoring Duchenne muscular dystrophy gene therapy with epitope-specific monoclonal antibodies -- Methods for noninvasive monitoring of muscle fiber survival with an AAV vector encoding the mSEAP reporter gene -- Monitoring murine skeletal muscle function for muscle gene therapy -- Phenotyping cardiac gene therapy in mice -- Golden retriever muscular dystrophy (GRMD): Developing and maintaining a colony and physiological functional measurements -- Directed evolution of adeno-associated virus (AAV) as vector for muscle gene therapy -- Systemic gene transfer to skeletal muscle using reengineered AAV vectors -- Bioinformatic and functional optimization of antisense phosphorodiamidate morpholino oligomers (PMOs) for therapeutic modulation of RNA splicing in muscle -- Engineering exon-skipping vectors expressing U7 snRNA constructs for Duchenne muscular dystrophy gene therapy -- Application of microRNA in cardiac and skeletal muscle disease gene therapy -- Molecular imaging of RNA interference therapy targeting PHD2 for treatment of myocardial ischemia -- Lentiviral vector delivery of shRNA into cultured primary myogenic cells: A tool for therapeutic target validation -- Fetal muscle gene therapy/gene delivery in large animals -- Electroporation of plasmid DNA to swine muscle -- Local gene delivery and methods to control immune responses in muscles of normal and dystrophic dogs -- Gene transfer to muscle from the isolated regional circulation -- AAV-mediated gene therapy to the isolated limb in rhesus macaques -- Antisense oligo-mediated multiple exon skipping in a dog model of Duchenne muscular dystrophy -- Whole body skeletal muscle transduction in neonatal dogs with AAV-9 -- A translatable, closed recirculation system for AAV6 vector-mediated myocardial gene delivery in the large animal -- Method of gene delivery in large animal models of cardiovascular diseases -- Percutaneous transendocardial delivery of self-complementary adeno-associated virus 6 in the canine.